Rare-disease organisations we work with
GeN works with patient organisations, academic groups, biotechnology companies and pharmaceutical partners to turn promising science into focused therapeutic programmes.
FRAXA Research Foundation
Fragile X syndrome · Drug Validation Initiative
Pitt Hopkins Research Foundation
Pitt–Hopkins syndrome research and preclinical development
Kabuki Syndrome Foundation
Disease-relevant research and therapeutic evaluation
For foundations
Define therapeutic questions and generate reproducible preclinical evidence
For academia
Translate mechanisms and discoveries into testable drug-development programmes
For pharma
Evaluate assets, strengthen translational packages and explore GE07 partnering
